Enzon sells specialty drug business for $300M Nov 10, 2009
The specialty drugs sigma-tau is buying are cancer drug Oncaspar, fungal infection treatment Abelcet, meningitis drug DepoCyt, and Adagen, which is used for severe combined immunodeficiency disease, or "Bubble Boy Disease.". In 2008, Enzon announced plans to spin off its biotechnology business into an independent company so it could focus on developing treatments for cancer. (Yahoo News -- Pharmaceutical Industry News)
Gene therapy halts brain disease Nov 6, 2009
Its development has suffered a number of setbacks, including the death 10 years ago of an American teenager in one experiment and two cases of leukemia in boys treated for severe combined immunodeficiency (SCID) in 2002. More recently, though, doctors have made encouraging steps. (MSNBC -- Health)
Gene Therapy Technique Slows Brain Disease ALD Featured In Movie 'Lorenzo's Oil' Nov 6, 2009
(May 16, 2006) Researchers from the University of Pennsylvania and NIAID have successfully restored the immune system in basset pups with X-linked severe combined immunodeficiency (the so-called "bubble-boy". (Feb. (Science Daily)
SCID Kids Leading Healthy, Normal Lives 25 Years After 'Bubble Boy' Oct 14, 2009
18, 2008) Severe combined immunodeficiency (SCID) is an inherited disease sometimes known as "boy in the bubble syndrome," because the patient lacks one or more type of immune cell, making them very ... 28, 2005) Two new studies show that newborn screening for Severe Combined Immunodeficiency (SCID) -- a rare, treatable disorder of the immune system commonly known as "bubble boy disease" -- is both ... 10, 2008) Severe combined immunodeficiency (SCID), sometimes called 'Boy in the bubble... (Science Daily)
School helps ailing toddler Mountain View High School rallies again to help the young daughter of two teachers May 27, 2009
Olivia has severe combined immunodeficiency syndrome, a disease which takes away her ability to fight off bacteria and infections. Olivia and her mother moved to Durham, N.C., last fall so she could be treated by doctors at Duke University Medical Center. (Fredericksburg.com, VA)
BIOTECH: Local stem cell scientists get $36M from state Apr 30, 2009
One of those is X-linked Severe Combined Immunodeficiency, or "bubble boy disease.". -- Jeanne Loring of The Scripps Research Institute to produce safety measures for stem cells being considered for human therapy. (North County Times)
Making Gene Therapy Safer Using Self-inactivating LTRs Apr 3, 2009
10, 2008) Severe combined immunodeficiency (SCID), sometimes called 'Boy in the bubble syndrome', is a genetic disorder in which the patient lacks most types of immune cell. Almost 10 years ago, two. (Science Daily)
Boy In The Bubble Remembered For Remarkable Legacy Feb 24, 2009
David had severe combined immunodeficiency, or SCID, an inherited condition in which someone lacks the white blood cells that fight infection. It afflicts 40 to 50 babies born every year in the United States and is fatal within a year or two without treatment. (KWTX.com, TX)
Restoring Function Of A Mutant Gene Without Altering DNA Might Be Possible Feb 13, 2009
18, 2008) Severe combined immunodeficiency (SCID) is an inherited disease sometimes known as "boy in the bubble syndrome," because the patient lacks one or more type of immune cell, making them very. . (Science Daily)
